A single infusion of the experimental CRISPR-Cas9 therapy CTX310 kept LDL cholesterol down 52.5% and triglycerides down 47.8% a year later in a first-in-human trial, with no serious treatment-related adverse events.
A gene therapy can turn certain brain glial cells into functioning neurons, which in turn could help repair the brain after a stroke or during neurological disorders like Alzheimer’s or Parkinson’s diseases. In a series of studies in animals, a... Continue Reading →